Orphan designation: Rimeporide Treatment of Duchenne muscular dystrophy, 26/02/2025 Positive
At the time of designation, DMD affected approximately 0.5 in 10,000 people in the European Union (EU). This was equivalent to a total of around 26,000 people*, and is below the ceiling for orphan designation, which is 5 people in 10,000. This isbased on …